Astrocyte Subtype Vulnerability in Stem Cell Models of Vanishing White Matter
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Affected astrocytes in the spinal cord of the leukodystrophy vanishing white matter
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Astrocytes are central in the pathomechanisms of vanishing white matter
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Leukoencephalopathy with vanishing white matter: a review
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Natural History of Vanishing White Matter
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Cell Replacement Therapy Improves Pathological Hallmarks in a Mouse Model of Leukodystrophy Vanishing White Matter
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Bergmann glia translocation: a new disease marker for vanishing white matter identifies therapeutic effects of Guanabenz treatment
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eIF2B activator prevents neurological defects caused by a chronic integrated stress response
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The small molecule ISRIB rescues the stability and activity of Vanishing White Matter Disease eIF2B mutant complexes
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Drug Screening Identifies Sigma-1-Receptor as a Target for the Therapy of VWM Leukodystrophy
Front Mol Neurosci. 2018;11:336. Published 2018 Sep 18. doi:10.3389/fnmol.2018.00336